Sep 30, 2024

Ultragenyx Q3 2024 Earnings Report

Ultragenyx reported a 42% increase in total revenue compared to the prior year, driven by growth in Crysvita and Dojolvi revenues, and provided updates on clinical milestones.

Key Takeaways

Ultragenyx reported a strong third quarter with a 42% increase in total revenue, reaching $139 million. Crysvita revenue grew by 31% to $98 million, and Dojolvi revenue increased by 29% to $21 million. The company reaffirmed its 2024 total revenue guidance of $530 million to $550 million and highlighted clinical advancements, including Breakthrough Therapy Designation for setrusumab.

Total revenue for Q3 2024 grew by 42% year-over-year to $139 million.

Crysvita revenue increased by 31% to $98 million, driven by growth in Latin America and Turkey.

Dojolvi revenue grew by 29% to $21 million.

Breakthrough Therapy Designation was granted for setrusumab (UX143) in osteogenesis imperfecta.

Total Revenue
$139M
Previous year: $98.1M
+42.3%
EPS
-$1.4
Previous year: -$2.23
-37.2%
Total Operating Expenses
$271M
Previous year: $243M
+11.7%
Gross Profit
$110M
Previous year: $87.1M
+26.0%
Cash and Equivalents
$825M
Previous year: $524M
+57.3%
Free Cash Flow
-$68.6M
Previous year: -$122M
-43.6%
Total Assets
$1.54B
Previous year: $1.24B
+24.2%

Ultragenyx

Ultragenyx

Ultragenyx Revenue by Segment

Forward Guidance

The company expects total revenue to be in the range of $530 million to $550 million, Crysvita revenue to be towards the upper end of the range of $375 million to $400 million, Dojolvi revenue to be in the range of $75 million to $80 million, and Net Cash Used in Operations of around $400 million for the full year 2024.

Positive Outlook

  • Total revenue to be in the range of $530 million to $550 million
  • Crysvita revenue to be towards the upper end of the range of $375 million to $400 million.
  • Crysvita revenue includes all regions where Ultragenyx will recognize revenue: product sales in Latin America and Turkey, royalties in Europe, which have been ongoing, and royalties in North America, which began in April 2023.
  • Dojolvi revenue to be in the range of $75 million to $80 million
  • Expect enrollment to be completed in the next few months for DTX301 AAV gene therapy for Ornithine Transcarbamylase (OTC) Deficiency

Challenges Ahead

  • Net Cash Used in Operations of around $400 million
  • Net loss of $134 million, or $1.40 per share basic and diluted
  • Operating expenses were $271 million
  • Net cash used in operations was $67 million
  • The company expects to enroll an additional cohort in Stage 1 at a moderately increased dose and with an optimized immunomodulation regimen to enhance the efficiency and efficacy of the gene therapy

Revenue & Expenses

Visualization of income flow from segment revenue to net income