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Dec 31, 2020

Ultragenyx Q4 2020 Earnings Report

Ultragenyx reported Q4 2020 financial results and provided a corporate update.

Key Takeaways

Ultragenyx reported total revenue of $91.5 million for the fourth quarter of 2020. The company had a net loss of $24.0 million, or $0.37 per share. They reaffirmed the 2021 guidance range for Crysvita of $180 million to $190 million.

Total revenue for the fourth quarter of 2020 was $91.5 million.

Crysvita revenue in Ultragenyx territories was $40.4 million for Q4 2020.

Dojolvi product sales were $6.4 million in the fourth quarter of 2020.

Net loss for the fourth quarter of 2020 was $24.0 million, or $0.37 per share.

Total Revenue
$91.5M
Previous year: $35.6M
+157.2%
EPS
-$0.37
Previous year: -$1.62
-77.2%
Gross Profit
$91.5M
Cash and Equivalents
$1.21B
Previous year: $760M
+59.4%
Free Cash Flow
-$84.4M
Total Assets
$1.76B
Previous year: $1.14B
+55.0%

Ultragenyx

Ultragenyx

Ultragenyx Revenue by Segment

Forward Guidance

The company reaffirms the 2021 guidance range for Crysvita that was provided at the beginning of the year. This range is $180 million to $190 million for the North American profit share region and the other regions where product sales are recognized (Latin America and Turkey).

Positive Outlook

  • Initiate a Phase 3 study for DTX401 for Glycogen Storage Disease Type Ia (GSDIa) in the first half of 2021.
  • Initiate a Phase 3 study for DTX301 for Ornithine Transcarbamylase (OTC) Deficiency in the second half of 2021.
  • Initiate a Phase 1/2/3 study for UX701 for Wilson disease in the first half of 2021.
  • Resume enrollment and dosing in the Phase 1/2 study for GTX-102 for Angelman Syndrome in the first half of 2021.
  • Conduct a Phase 2/3 study in pediatric patients for UX143 (setrusumab) for Osteogenesis Imperfecta, anticipated in second half of 2021.

Challenges Ahead

  • Uncertainty and potential delays related to clinical drug development.
  • Smaller than anticipated market opportunities for the company’s products and product candidates.
  • Manufacturing risks.
  • Competition from other therapies or products.
  • Effects from the COVID-19 pandemic on the company’s clinical activities, business and operating results.

Revenue & Expenses

Visualization of income flow from segment revenue to net income