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Dec 31, 2023
Rocket Q4 2023 Earnings Report
Rocket Pharmaceuticals reported financial results for Q4 2023, highlighting progress in its gene therapy programs and preparations for the launch of KRESLADI™.
Key Takeaways
Rocket Pharmaceuticals reported a net loss of $59.7 million for the fourth quarter of 2023. The company's cash, cash equivalents, and investments totaled $407.5 million as of December 31, 2023, expected to fund operations into 2026. Rocket is advancing its pipeline of gene therapies and preparing for the potential launch of KRESLADI™ for severe LAD-I.
Rocket Pharmaceuticals is on track for regulatory filings in Fanconi Anemia.
The company is progressing clinical programs in Danon Disease, PKP2-ACM, and PKD.
KRESLADI™ for severe LAD-I has a PDUFA date of June 30, 2024.
Rocket is expanding commercial capabilities to support the launch of its LV portfolio.
Rocket
Rocket
Forward Guidance
Rocket Pharmaceuticals expects its current cash reserves to fund operations into 2026, supporting the development of its clinical and preclinical programs and the production of AAV cGMP batches.
Positive Outlook
- Continued development of six clinical and/or preclinical programs.
- Production of AAV cGMP batches at the company’s Cranbury, N.J. R&D and manufacturing facility.
- Potential launch of KRESLADI™ for severe LAD-I.
- Regulatory filings for Fanconi Anemia remain on track.
- Advancement of clinical programs in Danon Disease, PKP2-ACM and PKD.
Challenges Ahead
- Dependence on third parties for development, manufacture, marketing, sales and distribution of product candidates.
- The outcome of litigation.
- Unexpected expenditures.
- Competitors’ activities, including decisions as to the timing of competing product launches, pricing and discounting.
- Ability to develop, acquire and advance product candidates into, enroll a sufficient number of patients into, and successfully complete, clinical studies.